According to the BBC News, experts are excited about possibly "the biggest breakthrough in neurodegenerative diseases for 50 years." An experimental drug has, for the first time, corrected a defect that causes Huntington's disease. Huntington's is a devastating disease that usually manifests in middle age, leading to a permanent decline in patients due to the unstoppable death of brain cells. Patients' movement, memory, and behavior are affected, causing an almost vegetative state eventually.
Huntington's is caused by an error in the DNA section called the huntingtin gene, a gene that makes a protein vital for brain development. The genetic error that occurs alters the protein and causes it to kill brain cells. The experimental drug that has been found to be effective by a research team at University College London is designed to silence that gene. Doctors are careful not to call this a cure, but they are very hopeful at the treatment's potential.
Click Read More for more detail from the BBC News.
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